Educating and Advocating

for People Affected by Sickle Cell

Two gene therapies were recently approved by the Food and Drug Administration (FDA) to treat sickle cell disease: Casegevy from CRISPR/Vertex and Lyfgenia from bluebird bio. You probably have questions about these new treatment options. Read more below. Is gene therapy a cure for sickle cell disease? Gene therapy is a potentially curative therapy. This The post Gene Therapy: What You Need to Know appeared first on Sickle Cell Disease Association of America Inc..